2022 RARE Patient Advocacy Summit

Breakthroughs That Change Patients' Lives: Pfizer is a leading research-based biopharmaceutical company. We apply science and our global resources to deliver innovative therapies that extend and significantly improve lives.

Ipsen is a global mid-size biopharmaceutical company with a focus on transformative medicines in Oncology, Neuroscience and Rare Disease. Under the overarching theme of Focus. Together.

We're passionate about finding solutions for people facing the world's most difficult-to-treat conditions. That is why we use cutting-edge science to create and deliver innovative medicines around the globe. To us, science is personal.

Sanofi is a global life sciences company committed to improving access to healthcare and supporting the people we serve throughout the continuum of care.

Astellas Pharma is a pharmaceutical company conducting business in more than 70 countries around the world.

The way we see it, the impossible is not impossible. It’s simply what hasn’t been achieved yet. For more than 30 years, we’ve pursued it, chased it down, tackled it for answers and surrounded it for a way in.

At Janssen, we never stop working toward a future where disease is a thing of the past.

Our mission is to transform the lives of people living with rare diseases and devastating conditions through the development and delivery of innovative medicines, as well as through supportive technologies and healthcare services.

At Horizon Therapeutics, we believe science and compassion must work together to transform lives.

"Jazz Pharmaceuticals plc (Nasdaq: JAZZ), is a global biopharmaceutical company whose purpose is to innovate to transform the lives of patients and their families.

Vertex is a global biotechnology company that invests in scientific innovation to create transformative medicines for people with serious and life-threatening diseases.

At Travere Therapeutics, our mission is to identify, develop and deliver life-changing therapies to people living with rare disease.

For more than 30 years, Ionis has been the leader in RNA-targeted therapy, pioneering new markets and changing standards of care with its novel antisense technology.

Chiesi Global Rare Diseases (GRD) is a business unit of the Chiesi Group, a global company with 85 years of experience in the pharmaceutical industry and operating in 29 countries.

We're focused on discovering and developing novel investigational medicines to treat genetically defined diseases through scientific leadership in the field of cellular metabolism.

At Ultragenyx, we fundamentally believe that taking real impactful action to care for the needs of patients and our people is always the right thing to do. To achieve this goal, our vision is to lead the future of rare disease medicine.

Get in the Ideas Business. At Regeneron we believe that when the right idea finds the right team, powerful change is possible.

Pharming is a specialty pharmaceutical company developing innovative products for the safe, effective treatment of rare diseases and unmet medical needs.

At Mallinckrodt, we use strategic vision and employee-driven momentum to pursue a powerful mission: Managing Complexity. Improving Lives.

Leadiant Biosciences, Inc. is a rare corporation dedicated to creating novel medicines for the unmet needs of patients with rare diseases.

At Harmony Biosciences, we specialize in developing and delivering treatments for rare neurological diseases that others often overlook.