Aditya Venkatesh

Senior Principal Scientist

Stoke Therapeutics Inc

Senior Principal Scientist

Stoke Therapeutics Inc
Andrew Kemp

Clinical Assistant Professor

University of Houston

Clinical Assistant Professor

University of Houston
Aprill Lane

US Advocacy Lead - Rare Disease

UCB

US Advocacy Lead - Rare Disease

UCB
Brian Mackness

Principal Scientist

Sanofi

Principal Scientist

Sanofi
Catherine Lawrence

Head of Rare Disease

Bionical Emas

Head of Rare Disease

Bionical Emas
Celine Gounder

Senior Fellow & Editor-at-Large for Public Health

Kaiser Health News

Senior Fellow & Editor-at-Large for Public Health

Kaiser Health News
David Dinh

Owner, Optometrist

Distinctive Vision Care

Owner, Optometrist

Distinctive Vision Care
Fernando Estrada

Lecturer in Immunology

University of Surrey

Lecturer in Immunology

University of Surrey
Francis Collins

Director

National Institutes of Health

Director

National Institutes of Health
James Warren

Vice President, Pharmaceutical Development

Ultragenyx Pharmaceutical Inc.

Vice President, Pharmaceutical Development

Ultragenyx Pharmaceutical Inc.
Jeremy Levin

Chairman Of The Board

Opthea

Chairman Of The Board

Opthea
Kate Tighe

VP, Head of US Public Affairs & Patient Advocacy - Rare Diseases

Sanofi

VP, Head of US Public Affairs & Patient Advocacy - Rare Diseases

Sanofi